A Family Guide to Non-Oncologic Blood Disorders
How successful is the treatment? Medications and IVIG can temporarily keep children with WAS healthy, but almost all patients with WAS will require stem cell transplant. To provide the best chances for success, a transplant is usually performed using the bone marrow or cord blood of a sibling. Some children do not have family members who are suitable donors in which case, doctors may use stem cells from an unrelated donor. The likelihood of a good outcome also is greater if the trans- plant is done early in life, if possible. Stem Cell Transplant Indications SCT provides WAS patients with healthy, blood-forming cells that will make normal platelets, T cells and B cells for the body. It is a cure for the disease and is highly effective in the majority of patients.
• Immediate referral to a pediatric immunologist (a doctor who specializes in the treatment of the immune system) • Basic precautions » » Avoid large crowds, dirty environments, and sick people. » » Strict handwashing » » Antibiotics, antifungal, and antiviral medications to treat any active infections or for prevention • Intravenous immune globulin (IVIG) is given to provide temporary antibodies that help protect your child from infections. • Platelet and/or blood transfusions • Medications (antibiotics and steroids) • Splenectomy to remove the spleen to increase the num- ber of platelets Your medical team will determine the best treatment plan for your child.
Notes from Your Child’s Medical Team
Wiskott Aldrich Syndrome
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