A Family Guide to Non-Oncologic Blood Disorders
Stem Cell Transplant Indications SCT replaces the abnormal cells in the bone marrow (the cells with the mutated gene) with healthy cells from a family mem- ber, an unrelated donor, or a cord blood unit. The healthy cells provide a source of the enzyme needed to break down GAGs and stop further damage to the body.
complications from transplant is higher. In addition, a trans- plant may not undo damage the disease has already done, especially to the nervous system. Your child will need to be treated for the medical issues that already exist.
Notes from Your Child’s Medical Team
Hurler Syndrome
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